Publication
Direct delivery of Cas9 or base editor protein and guide RNA complex enables genome editing in the retina.
Molecular therapy. Nucleic acids
Pulman J, Botto C, Malki H, Ren D, Oudin P, De Cian A, As M, Izabelle C, Saubamea B, Forster V, Fouquet S, Robert C, Portal C, El-Amraoui A, Fisson S, Concordet JP, Dalkara D